Backed by a handful of prominent investors including the Gates Foundation, the startup is pursuing an approach it believes ...

A new class of life-saving drugs is helping children who once had no hope. But some carry a price tag of millions for a ...

Researchers hoped they had finally found a way to get gene therapies past the blood-brain barrier. Then the first patient ...

JABSOM Cell and Molecular Biology researcher Dr. Jesse Owens has spent the better part of two decades chasing a vision that ...

Major is one of the first pediatric patients in Florida to receive gene therapy for sickle cell disease since the FDA ...

The FDA has issued its stamp of approval to a new, cell-based option to treat Wiskott-Aldrich syndrome (WAS), marking the ...

Aradigm Health, a new benefits platform aimed at easing the financial sting of coverage for cell and gene therapies, has ...

Cure Rare Disease (CRD) announced it has been awarded a $7.4 million grant from the California Institute for Regenerative ...

Investor optimism has waned as final minutes from uniQure’s pre-BLA meeting with the FDA convey that data from the company’s ...

A cutting-edge base-edited CAR T-cell therapy is opening a revolutionary new frontier for patients battling aggressive T-cell ...

Qalsody is one step closer to being covered by public Canadian healthcare systems when used to treat adults with ALS with ...

A long-term, trust-based CDMO partnership can support cell and gene therapy developers from early process development through ...